Gene Therapies for Neurological Diseases
The report explores how leading developers, emerging technologies, and strategic collaborations are shaping the next generation of therapies capable of addressing complex central nervous system (CNS) disorders. From AI-engineered AAV capsids to epigenetic editing platforms and non-viral delivery systems, it provides a detailed analysis of where innovation and investment are accelerating. Whether your focus is scientific advancement, market positioning, or partnership strategy, this report offers the intelligence you need to stay ahead in neurological gene therapy.
Key insights:
- Comprehensive landscape overview: 832 active assets targeting neurological disorders, accounting for 24.7% of all gene therapy programs tracked globally.
- Clinical momentum: 29 new trials and 22 new drug programs.
- Technology innovation: In-depth analysis of AAV9 and next-generation capsids, non-viral delivery platforms, and gene editing advancements including CRISPR and epigenetic systems.
- Market and partnership activity: Latest deals, collaborations, and restructuring moves from leading developers such as Sarepta, Regenxbio, Roche, and AbbVie.
- Future outlook: Emerging technologies and assets to watch – and how they’re poised to transform the treatment landscape for neurological diseases.
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Learn More About Gene Therapy
- The Most Comprehensive Way to Search the Gene Therapy Development Landscape: Unique search ontologies based on Gene Therapy drug and trial characteristics
- Market Leading Approach to Gene Therapy Preclinical & Clinical Data Curation: Manual curation of key Gene Therapy research and development data points by Gene Therapy research scientists
- Seamlessly Integrate Commercial & Scientific Data all in One Place: Search Gene Therapy company and deal data based on their pipeline and technologies.
- Unrivalled Granularity in Reports & Analysis: Our search ontology and technology indexing enable comprehensive analysis not seen elsewhere.
What is Beacon?
Beacon is a world leading data analysis tool for preclinical and clinical trial information. With unrivalled granularity of search function, data quality, and exhaustiveness, Beacon provides timely information and gives you confidence to progress your targeted drug therapies to patients.
Learn more about how our clinical trials and drug database solutions can be tailored to your research requirements
